With thousands of rare diseases affecting millions of families worldwide, one Tampa Bay lawmaker is taking action to position Florida as a national leader in genetic medicine.

Genetics plays a crucial role in the manifestation and progression of over 6,800 rare diseases, including but not limited to, genetic disorders, rare ...

Danon disease is a rare but serious cardiomyopathy that drastically reduces life expectancy. Male patients infrequently live ...

I want Kevin Kiley to meet her face-to-face and tell us why he won’t support these programs,” said Frances Pimentel, the ...

A mother has spoken about her "painful" experience over the potential end to her son's life-enhancing treatment for a rare ...

If successful, the genetic modification developed by the Transmission Zero team could provide a long-term solution by ...

A recent review published in the journal Engineering delves into the significant advancements and potential of CRISPR ...

In 2025, Cellectis will continue to focus its efforts and expenses on advancing its core clinical trials BALLI-01 and NATHALI ...

A Shreveport-Bossier City musician is working tirelessly to better the quality of life for people like her sons, some of whom ae fighting a challenging disease.

Nexus Health Systems serves niche populations. This approach to health care enables Dr. Cassidy to address rare illnesses ...

Researchers from the University of Jyväskylä, Finland, investigated the links between long-term leisure-time physical ...